Longitudinal Study of Urea Cycle Disorders

计划入组 1,500 人 · 首次发布于 2005 年 10 月 12 日

Neuroimaging and Neuropsychological Outcomes in Urea Cycle Disorders

计划入组 56 人 · 首次发布于 2016 年 10 月 17 日

Pilot Study: Urea Cycle Disorders Practice Patterns and Outcomes Assessment

计划入组 87 人 · 首次发布于 2014 年 12 月 8 日

Urea cycle disorders(CAMP4 Therapeutics)

RNA actuator therapeutic (urea cycle disorder)

Glycerol phenylbutyrate(Ravicti)

C₃₃H₃₈O₆ · Rx

Zevra Therapeutics

United States

CYCLE PHARMACEUTICALS LTD

United Kingdom

Cycle Pharmaceuticals Ltd.

United States

Endo Launches First Generic Version of RAVICTI for Rare Urea Cycle Disorders

Ravicti Receives Regulatory Approval in Saudi Arabia, Qatar, and Kuwait for Urea Cycle Disorders

Citrin Foundation and University Children's Hospital Zürich Launch Pioneering Center for Urea Cycle Disorders Research