Gene Therapy for Wiskott-Aldrich Syndrome (WAS)

计划入组 6 人 · 首次发布于 2011 年 5 月 4 日

Post-transplant Cyclophosphamide in Wiskott-Aldrich Syndrome

计划入组 5 人 · 首次发布于 2017 年 6 月 26 日

Patients Treated for Wiskott-Aldrich Syndrome (WAS) Since 1990

计划入组 305 人 · 首次发布于 2014 年 2 月 17 日

Wiskott-Aldrich Syndrome therapy (ImmunoVec)

Wiskott-Aldrich syndrome gene therapy (Genethon)

Wiskott-Aldrich syndrome gene therapy(Généthon)

ALPORT SYNDROME FOUNDATION

United States

International Rett Syndrome Foundation

United States

RETT SYNDROME RESEARCH TRUST

United States

EMA Recommends First Gene Therapy for Wiskott-Aldrich Syndrome

FDA Approves First Gene Therapy for Wiskott-Aldrich Syndrome

Telethon Foundation Seeks EMA Approval for Etuvetidigene Autotemcel in Wiskott-Aldrich Syndrome