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找到 10,690 条关于
“alpha-A1 antitrypsin deficiency”
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10,690
临床试验
7,615
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1,266
机构
21
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1,788
2年前
BridgeBio Refocuses on Late-Stage Assets, Trims Pipeline to Sharpen Commercial Focus
去年
Intellia Therapeutics Initiates Phase 1/2 Trial of NTLA-3001 for AATD-Associated Lung Disease
去年
Beam Therapeutics Achieves Breakthrough in Base Editing for Alpha-1 Antitrypsin Deficiency
去年
FDA Approves Larger Vial Sizes of Takeda's GLASSIA for Alpha-1 Antitrypsin Deficiency
去年
UT Southwestern Scientists Develop Targeted Gene Therapy for Alpha-1 Antitrypsin Deficiency Using Designer Lipid Nanoparticles
9个月前
Regeneron Partners with Tessera in $275M Gene Editing Deal for Alpha-1 Antitrypsin Deficiency Treatment
11个月前
Sanofi's Efdoralprin Alfa Achieves Primary Endpoints in Phase 2 Alpha-1 Antitrypsin Deficiency Study
去年
Novel Therapies Poised to Revolutionize Alpha-1 Antitrypsin Deficiency Treatment
去年
Prime Medicine Advances Gene Editing Program for Alpha-1 Antitrypsin Deficiency with 72% Correction Rate
7个月前
YolTech's YOLT-202 Gene Editing Therapy Shows Promising Results in Alpha-1 Antitrypsin Deficiency Trial
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