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找到 684 条关于
“antisense”
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684
临床试验
228
药物
177
机构
6
资讯
273
去年
Antisense Oligonucleotide Therapies Advance in Genetic Medicine
2个月前
Antisense Oligonucleotides: Rewriting the Future of Rare Inherited Genetic Diseases
去年
Vanda Pharmaceuticals' VGT-1849A, a Selective JAK2 Inhibitor, Receives FDA Orphan Drug Designation for Polycythemia Vera
9个月前
Antisense Oligonucleotide Therapy Reverses Developmental Defects in Spinal Muscular Atrophy Organoids
10个月前
Aperture Therapeutics Advances CD33-Targeting Antisense Oligonucleotide APRTX-001 for Neurodegenerative Diseases
去年
SynaptixBio Selects Antisense Oligonucleotide Candidate for Rare Disease H-ABC Clinical Trials
2年前
VO659 Shows Promise in Reducing Mutant Huntingtin Protein in Huntington's Disease Patients
6个月前
SpliSense Receives EMA e-PRIME Designation for SPL84 Antisense Therapy in Cystic Fibrosis
上个月
Researchers Uncover CD44–EPHA2 Endosomal Pathway That Could Unlock Antisense Therapy for Cancer
去年
SpliSense Achieves First Positive Phase 2 Results for Inhaled Antisense Therapy in Cystic Fibrosis
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