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找到 79,116 条关于
“antisense oligonucleotide therapy”
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79,116
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9个月前
Antisense Oligonucleotide Therapy Reverses Developmental Defects in Spinal Muscular Atrophy Organoids
11天前
Aptar and Aceso Therapeutics Partner to Advance Inhaled Antisense Oligonucleotide Therapy for Cystic Fibrosis
2个月前
Vanda Pharmaceuticals Secures FDA Rare Pediatric Disease Designation for Antisense Oligonucleotide Therapy VCA-894A in CMT2S
去年
SpliSense Achieves First Positive Phase 2 Results for Inhaled Antisense Therapy in Cystic Fibrosis
去年
AusperBio Receives China CDE Clearance for Phase III Trial of Hepatitis B Antisense Therapy AHB-137
去年
Vanda Pharmaceuticals Initiates First-in-Human Trial of Personalized ASO Therapy VCA-894A for Ultra-Rare CMT2S
2年前
VO659 Shows Promise in Reducing Mutant Huntingtin Protein in Huntington's Disease Patients
21天前
AusperBio Completes $120 Million Series C to Advance AHB-137 Toward Commercialization in Chronic Hepatitis B
去年
CIRM Awards $5.69M Grant to Advance Novel Gene Therapy for Spinocerebellar Ataxia Type 3
6个月前
SpliSense Receives EMA e-PRIME Designation for SPL84 Antisense Therapy in Cystic Fibrosis
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