Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency

计划入组 154,795 人 · 首次发布于 2015 年 3 月 26 日

An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.

计划入组 6 人 · 首次发布于 2023 年 3 月 13 日

A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion

计划入组 12 人 · 首次发布于 2016 年 10 月 6 日

Aromatic l-amino acid decarboxylase deficiency gene therapy (Gene Therapy Research Institution)

Eladocagene exuparvovec(Upstaza)

oxalate decarboxylase

Shanghai Ajinomoto Amino Acid Co., Ltd.

China

AMINO GmbH

Germany

CLEVELAND CLINIC ABUDHABI L L C

United Arab Emirates

FDA Approves PTC Therapeutics' Kebillidi, First Gene Therapy for AADC Deficiency

FDA Approves Kebilidi, First Gene Therapy for AADC Deficiency

FDA Approves Kebilidi, First Gene Therapy for AADC Deficiency