Bullying in Youth With Muscular Dystrophy and Congenital Myopathies

计划入组 29 人 · 首次发布于 2021 年 2 月 2 日

Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I

计划入组 38 人 · 首次发布于 2014 年 6 月 17 日

HBCMD01- Expanded Access for the Treatment of Congenital Muscular Dystrophy.

首次发布于 2021 年 12 月 13 日

Genetic Muscular Dystrophy program

muscular dystrophy therapeutic

Muscular Dystrophy(SKIP)

Dyne Therapeutics

United States

Sarepta Therapeutics, Inc.

United States

PEGBIO CO-B

FDA Grants Orphan Drug Designation to MDL-101 for Congenital Muscular Dystrophy Type 1A

FDA Grants Orphan Drug Designation to Modalis Therapeutics' MDL-101 for LAMA2-CMD

Modalis Therapeutics Receives FDA Orphan Drug Designation for MDL-101 in LAMA2-CMD Treatment