A Study of VPRIV in Participants With Gaucher Disease Previously Treated With Other Enzyme Replacement Therapies or Substrate Reduction Therapies

计划入组 2 人 · 首次发布于 2019 年 9 月 18 日

Study to Compare the Efficacy and Safety of Enzyme Replacement Therapies Avalglucosidase Alfa and Alglucosidase Alfa Administered Every Other Week in Patients With Late-onset Pompe Disease Who Have Not Been Previously Treated for Pompe Disease

计划入组 101 人 · 首次发布于 2016 年 5 月 25 日

Ophthalmic Findings During 10-year Enzyme Substitution of Danish Fabry Patients.

计划入组 39 人 · 首次发布于 2013 年 11 月 28 日

enzyme/protein replacement thyerapy

enzyme replacement therapy (biOasis)

Chaperone + RhIDUA Enzyme Replacement Therapy (Amicus Therapeutics)

AMANO ENZYME INC.

Japan

COLORADO JOINT REPLACEMENT

United States

OS Therapies

United States

China Approves First Domestically Developed Enzyme Replacement Therapy for Gaucher Disease

Pompe Disease Pipeline Shows Promise with Novel Therapies in Development

Global Regulatory Landscape for Psoriasis and Pompe Disease Treatments Evolving in 2025