The Natural History of Familial Dysautonomia

计划入组 400 人 · 首次发布于 2019 年 4 月 19 日

The Nutritional Supplement Phosphatidylserine in Patients With Familial Dysautonomia

计划入组 26 人 · 首次发布于 2014 年 10 月 28 日

Telemedicine Clinical Trial for Cognitive Behavioral Therapy in Familial Dysautonomia

首次发布于 2019 年 4 月 10 日

Adeno-Associated Virus serotype 2 therapy (familial dysautonomia)

familial hypercholesterolemia program

VRX-LDLR

The Familial Hypercholesterolemia Foundation

United States

Madrigal Pharmaceuticals

United States

FUNDACION HIPERCOLESTEROLEMIA FAMILIAR

Spain

FDA Awards Dual Designations to Tikun's Novel Familial Dysautonomia Treatments

FDA Expands Rare Disease Research Support with $27 Million in Grants and New Innovation Hub

Homozygous Familial Hypercholesterolemia Treatment Market to Surge by 2034