Registry of Patients Diagnosed With Lysosomal Storage Diseases

计划入组 250 人 · 首次发布于 2022 年 11 月 17 日

Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children

计划入组 19 人 · 首次发布于 2013 年 9 月 10 日

Molecular and Cellular Mechanisms of Lysosomal Storage Diseases

计划入组 80 人 · 首次发布于 2013 年 12 月 4 日

Lysosomal storage disease therapeutics (bioOasis)

Lysosomal storage disease 2(Belief Biomed)

Lysosomal Storage Disease Therapeutics(Orphazyme Aps)

Self Storage Group Inc

United States

Rare Disease Research, LLC

LYSOSOMAL AND RARE DISORDERS RESEARCH AND TREATMENT CENTER, INC.

United States

Polaryx Therapeutics Secures Nasdaq Listing Ahead of Phase 2 Trial for Rare Lysosomal Storage Disorders

GC Biopharma and Hanmi Pharmaceutical's Fabry Disease Treatment LA-GLA Receives FDA IND Clearance

Denali's Hunter Syndrome Candidate Receives FDA Orphan Drug and Rare Pediatric Disease Designations