Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy

计划入组 2 人 · 首次发布于 2015 年 3 月 3 日

A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)

计划入组 4 人 · 首次发布于 2017 年 12 月 15 日

Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy

计划入组 6 人 · 首次发布于 2007 年 1 月 30 日

rAAVrh74.MCK.Micro-Dystrophin

micro-utropin

Micro-Release

Protein Sciences Corporation

United States

MICRO LABS LIMITED

India

Micro-Macinazione SA

Switzerland

Sarepta's Elevidys Receives Full FDA Approval for Expanded Use in Duchenne Muscular Dystrophy

FDA Approves Elevidys, a Gene Therapy for Duchenne Muscular Dystrophy

Sarepta Receives FDA Approval for Enhanced ELEVIDYS Gene Therapy Trial in Non-Ambulatory Duchenne Patients