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找到 10,469 条关于
“nonsense mutation DMD”
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10,469
临床试验
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88
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3年前
EMA Panel Recommends Against Renewing Translarna Approval for Duchenne Muscular Dystrophy
7个月前
PTC Therapeutics Withdraws Translarna NDA for Duchenne Muscular Dystrophy Following FDA Feedback
7个月前
Keros Therapeutics Advances KER-065 for Duchenne Muscular Dystrophy Following FDA Orphan Drug Designation
2个月前
PTC Therapeutics Launches Sephience for PKU with $125M in Q1 Sales and $500M Convertible Note Offering
去年
FDA Accepts Resubmitted NDA for Ataluren in Nonsense Mutation Duchenne Muscular Dystrophy
去年
FDA Accepts Resubmission of Translarna NDA for Nonsense Mutation Duchenne Muscular Dystrophy
2年前
FDA Accepts PTC Therapeutics' Translarna NDA Resubmission for Nonsense Mutation Duchenne Muscular Dystrophy
9天前
Tevard Biosciences Publishes Preclinical Data on Engineered Suppressor tRNA Gene Therapy for Duchenne Muscular Dystrophy
2年前
EMA Confirms Recommendation Against Renewing Translarna for Duchenne Muscular Dystrophy
12个月前
DEBRA Research and Nonsense Therapeutics Form ReadOn Therapeutics to Advance Epidermolysis Bullosa Treatments
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