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找到 73,290 条关于
“rare metabolic disorders”
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73,290
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去年
NIH Grant Funds Gene-Editing Research for Rare Metabolic Disorders
11个月前
NIH Awards $15.6 Million to Advance Research on Rare Bone and Metabolic Disorders
8个月前
Sanofi Secures Chinese Approval for Two Breakthrough Therapies Targeting Rare Cardiovascular and Metabolic Disorders
去年
Breakthrough Gene Editing Therapy Successfully Treats Infant with Rare Metabolic Disorder
9个月前
First-Ever Personalized CRISPR Therapy Successfully Treats Baby with Ultra-Rare Metabolic Disorder
去年
Applied Therapeutics to Present Extended INSPIRE Trial Data for Govorestat in SORD Deficiency at PNS Annual Meeting
去年
Relief Therapeutics Receives $2 Million Milestone Payment After FDA Approval of Arimoclomol
6个月前
Ono Pharmaceutical Expands AI-Driven Drug Discovery Into Neurology and Immunology Through Strategic Partnerships
去年
Maastricht UMC+ Develops Promising Drug for Hereditary Fructose Intolerance Treatment
去年
Lipocine's LPCN 2401 Demonstrates Significant Body Composition Improvements in Obesity Study
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