Early Diagnosis and Stem Cell Transplantation for Severe Immunodeficiency Diseases

计划入组 25 人 · 首次发布于 2008 年 2 月 13 日

Gene Therapy for X Linked Severe Combined Immunodeficiency

计划入组 10 人 · 首次发布于 2020 年 2 月 27 日

Gene Therapy for X-linked Severe Combined Immunodeficiency

计划入组 5 人 · 首次发布于 2011 年 8 月 4 日

stem cell gene therapy (X-linked severe combined immunodeficiency)

RAG1 CRISPR/Cas9 gene therapy (severe combined immunodeficiency disease)

Firolimogene autotemcel

NATIONAL INSTITUTE OF DISEASES OF THE CHEST AND HOSPITAL

Bangladesh

Theratechnologies

MediWound

Israel

FDA Approves Emergent BioSolutions' ACAM2000 for Mpox Prevention in High-Risk Individuals

FDA Grants Priority Review for Leniolisib in Children with Rare Immunodeficiency APDS

Kedrion Biopharma Secures FDA Approval for QIVIGY, First Proprietary IVIG Therapy for Primary Immunodeficiency