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找到 99,607 条关于
“sickle cell disorders”
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99,607
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5个月前
Scientists Win $3 Million Prize for Breakthrough Research Leading to First CRISPR Sickle Cell Therapy
5个月前
Scotland Launches First UK Newborn Screening Program for Spinal Muscular Atrophy
2个月前
FDA Approves ENNUMO™ (pegfilgrastim-pccg), Accord BioPharma's Second Pegfilgrastim Biosimilar to Neulasta
2年前
FDA Approves Gene Therapies Casgevy and Lyfgenia for Sickle Cell Disease
去年
Rigel's Fostamatinib Enrolls First Patient in Phase I Sickle Cell Disease Trial
去年
First Sickle Cell Patient Cured with Base Editing Gene Therapy
去年
Agios Pharmaceuticals Advances Tebapivat for Sickle Cell Disease and Hemolytic Anemias
去年
Beam Therapeutics' Base Editing Shows Promise in Sickle Cell Disease, Faces Safety Concerns
去年
Young Sickle Cell Patient Pioneers New Gene Therapy
3年前
CRISPR Gene Therapies Show Promise in Early Sickle Cell Disease Trials
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