BOEHRINGER INGELHEIM HELLAS SINGLE MEMBER S.A.

Greece

Rare Disease Research, LLC

CASTLEMAN DISEASE COLLABORATIVE NETWORK

United States

CURE RARE DISEASE, INC.

United States

Neurodegenerative Disease Research Inc

United States

Beyond Batten Disease Foundation

United States

Tropical Disease Foundation, Inc.

Philippines

Infectious Disease Research Institute

United States

Rare Disease Therapeutics, Inc.

United States

DIGESTIVE DISEASE RESEARCH INSTITUTE

Iran