Biomarker for the Early Diagnosis and Monitoring in Tyrosinemia Type 1 (BioTyrosin)

首次发布于 2017 年 9 月 15 日

Taste and Palatability of Orfadin Suspension

计划入组 18 人 · 首次发布于 2012 年 11 月 28 日

A Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in HT-1 Patients

计划入组 15 人 · 首次发布于 2024 年 1 月 26 日

Nitisinone(Nityr, Orfadin)

C₁₄H₁₀F₃NO₅ · Rx

FAH gene therapy (lentiviral vector, tyrosinemia type I )

Poliovirus type 1 antigen (formaldehyde inactivated)(Ipol, Kinrix, Pediarix, Pentacel, Quadracel, Vaxelis)

NHI-1

United States

Xi'an No.1 Hospital

China

ALPHA-1 FOUNDATION, INC.

United States

Nitisinone Shows Promise as Novel Malaria Control Strategy by Making Human Blood Lethal to Mosquitoes

Faeth Therapeutics Raises $25M to Advance PIKTOR Therapy After 80% Response Rate in Endometrial Cancer

Gilead's Lenacapavir Shows Promise in HIV Prevention, While GLP-1s Studied for Type 1 Diabetes