EUCTR2018-002935-88-DE进行中（未招募）1 期
A Long-term Follow-up Study of Subjects With ß-thalassemia or Sickle Cell Disease Treated with Autologous CRISPR-Cas9 Modified Hematopoietic Stem Cells (CTX001)
适应症
试验速览
- 阶段
- 1 期
- 状态
- 进行中（未招募）
- 入组人数
- 160
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Interventional clinical trial of medicinal product
入排标准
- 性别
- All
入选标准
- •1. Subjects (or his or her legally appointed and authorized
- •representative or guardian) must sign and date informed consent form
- •(ICF) and, where applicable, an assent form.
- •2. Subjects must have received CTX001 infusion in a parent study.
- •Are the trial subjects under 18? yes
- •Number of subjects for this age range: 34
- •F.1.2 Adults (18-64 years) yes
- •F.1.2.1 Number of subjects for this age range 80
- •F.1.3 Elderly (>=65 years) no
- •F.1.3.1 Number of subjects for this age range
排除标准
- •1. There are no exclusion criteria.
研究者
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