JPRN-UMIN000042872已完成未知
Development and evaluation of Gaucher disease (GD) - specific patient reported outcome measurement (PROM) in Japan. - Development and evaluation of Gaucher disease (GD) - specific patient reported outcome measurement (PROM) in Japan.
适应症
试验速览
- 阶段
- 未知
- 状态
- 已完成
- 入组人数
- 8
研究概览
简要总结
Three main themes emerged from qualitative analysis of patient interviews: treatment status, patient burden, and social support systems. Commonly used words and the relationships between words identified through the hierarchical cluster and co-occurrence network analyses supported these themes and topics. These themes and topics were specific to patients with types 2 and 3 GD and will be used to inform the development of a HRQOL questionnaire specifically for patients with all GD types
研究设计
- 研究类型
- Observational
入排标准
- 年龄范围
- ot applicable 至 ot applicable（—）
- 性别
- All
入选标准
- 未提供
排除标准
- •Patients: - Patients who have cognitive disabilities, - Patients who lack of fluency in Japanese. Caregivers: - Persons with cognitive disabilities - Persons with lack of fluency in Japanese
研究者
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