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临床试验/JPRN-UMIN000009392
JPRN-UMIN000009392招募中2 期

An Open-Label, Dose Escalation, Proof-of-Concept Clinical Trial of Chaperone therapy of Neuronopathic Gaucher Disease with Ambroxol - Chaperone therapy of Neuronopathic Gaucher Disease with Ambroxol

Tottori University, Faculty of Medicine, Institute of Neurological Science0 个研究点目标入组 5 人开始时间: 2012年11月24日最近更新:
适应症

试验速览

阶段
2 期
状态
招募中
发起方
入组人数
5

研究概览

简要总结

暂无简介。

研究设计

研究类型
Interventional

入排标准

年龄范围
ot applicable 至 ot applicable(—)
性别
All

入选标准

  • 未提供

排除标准

  • 1) Patients with critical illness 2) Pregnant or lactating woman 3) Within 3 months from other clinical trial 4) Patients who are not appropriate to participate to the trial.

研究者

发起方
Tottori University, Faculty of Medicine, Institute of Neurological Science

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