EUCTR2014-003644-12-DK进行中（未招募）1 期
The effect of Triheptanoin in adults with McArdle Disease (Glycogen Storage Disease Type V) - Triheptanoin in McArdle
euromuscular Research Unit, Rigshospitalet0 个研究点目标入组 28 人开始时间: 2014年11月4日最近更新:
适应症
试验速览
- 阶段
- 1 期
- 状态
- 进行中（未招募）
- 发起方
- 入组人数
- 28
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Interventional clinical trial of medicinal product
入排标准
- 性别
- All
入选标准
- •- Age > 18 years
- •- Age < 75 years
- •- Genetically and/or biochemically verified diagnosis of McArdle disease
- •- Body Mass Index of 18-32
- •- Capacity to consent
- •- Women in fertile age on contraceptive treatment with: Birth control pills, coil, ring, transdermal hormone patch injection of gestagen or subdermal implant.
- •Are the trial subjects under 18? no
- •Number of subjects for this age range:
- •F.1.2 Adults (18-64 years) yes
- •F.1.2.1 Number of subjects for this age range 28
- •F.1.3 Elderly (>=65 years) no
- •F.1.3.1 Number of subjects for this age range
排除标准
- •- Significant cardiac or pulmonary disease
- •- Pregnancy (confirmed by plasma-HCG) or breastfeeding.
- •- Inability to perform cycling exercise
- •- Any other significant disorder that may confound the interpretation of the findings
研究者
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