NL-OMON49948招募中不适用
10-year extension study: prospective systematic follow-up for X-linked adrenoleukodystrophy. - Prospective follow-up in X-ALD.
适应症
试验速览
- 阶段
- 不适用
- 状态
- 招募中
- 入组人数
- 200
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Observational invasive
入排标准
- 年龄范围
- 0 至 64（—）
入选标准
- •In order to be eligible to participate in this study, a subject must meet all
- •of the following criteria:
- •- Diagnosis of ALD (confirmed by ABCD1 mutation analysis)
- •- For male patients: Willing to undergo regular follow-up visits (twice yearly
- •if <12 years and yearly if > 12 years) with blood sampling and MRI scan of the
- •- For female patients: Willing to visit the hospital once every two to three
- •- Provision of written informed consent to participate in the study obtained
- •from the participant or legal guardian in case of a minor
- •Subjects eligible to participate as healthy controls must meet all of the
- •following criteria:
- •- Willing to visit the hospital
- •- 16 years or older
- •- Provision of written informed consent to participate in the study obtained
- •from the participant
排除标准
- •A potential subject (patient or healthy control) who meets any of the following
- •criteria will be excluded from participation in this study:
- •- unable to visit the hospital for follow up (for example in case of advanced
- •- co existing neurological disease making interpretation of acquired data
- •difficult (for instance multiple sclerosis)
研究者
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