DRKS00025852已完成不适用
Survival analysis of Acid Sphingomyelinase deficiency (ASMD) among German patients during childhood to adulthood: a retrospective chart review study - SURGE
适应症
试验速览
- 阶段
- 不适用
- 状态
- 已完成
- 入组人数
- 33
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Observational
入排标准
- 年龄范围
- one 至 one（—）
- 性别
- All
入选标准
- •I 01.Pediatric, adolescent and adult ASMD (surviving and deceased) patients with retrievable information from German hospital medical records between January 1st 1990 and July 31st 2021.
- •I 02.A first date of evidence of ASMD defined as either first symptom onset or a diagnosis of ASMD Type B or A/B, whichever comes first. This first date of evidence of ASMD to be defined as the index date.
- •I 03.Patient and/or patient’s parent/legal guardian must provide informed assent/consent.
排除标准
- •E 01. Patients with no retrievable information from the medical record
- •E 02. Patients with ASMD type A
研究者
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