JPRN-jRCT2033220245招募中未知
ong-term observational study of Gene Therapy for AADC deficiency
Yamagata Takanori0 个研究点目标入组 1 人开始时间: 2022年8月5日最近更新:
适应症
试验速览
- 阶段
- 未知
- 状态
- 招募中
- 发起方
- 入组人数
- 1
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Observational
入排标准
- 年龄范围
- ot applicable 至 ot applicable（—）
- 性别
- All
入选标准
- •Patients who enrolled in the Phase I/II Study of Gene Therapy for AADC deficiency, and who completed or discontinued the study.
- •-Female patients who are able to become pregnant, and whose partners agree to use medically effective contraceptive methods throughout the study period.
排除标准
- •-Patients who cannot undergo MRI.
研究者
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