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Exon 53
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Exon 53
Exon 53
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临床试验
审批记录
专利
每项发明一条,涵盖美国、欧洲、PCT 与中国的同族专利。
EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
EP 3554552 A1
申请人: SAREPTA THERAPEUTICS INC
优先权: 2016
CN
EP
US
WO
9 件公开
METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50-53
US 2011263682 A1
申请人: ACADEMISCH ZIEKENHUIS LEIDEN
优先权: 2007
CN
EP
US
6 件公开
Modulation of exon recognition in pre-mRNA by interfering with the secondary RNA structure
US 10113165 B2
申请人: ACADEMISCH ZIEKENHUIS LEIDEN
优先权: 2014
US
5 件公开
EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
EP 3495485 A3
申请人: SAREPTA THERAPEUTICS INC
优先权: 2013
CN
EP
US
4 件公开
EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
EP 3784248 A2
申请人: SAREPTA THERAPEUTICS INC
优先权: 2018
EP
US
WO
4 件公开
US 20250090569 A1
申请人: SAREPTA THERAPEUTICS INC
优先权: 2024
US
Effective gene therapy tools for dystrophin exon 53 skipping
US 10752898 B2
申请人: GENETHON
优先权: 2015
CN
EP
US
3 件公开
OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
EP 3790596 A1
申请人: WAVE LIFE SCIENCES LTD
优先权: 2018
CN
EP
WO
3 件公开
PRECISE EXCISIONS OF PORTIONS OF EXON 44, 50, AND 53 FOR TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY
EP 4490292 A1
申请人: VERTEX PHARMA
优先权: 2022
EP
US
WO
3 件公开
IMPROVED EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
EP 3885439 A1
申请人: SAREPTA THERAPEUTICS INC
优先权: 2012
CN
EP
3 件公开
Medicament for treatment of Duchenne muscular dystrophy
US 6653467 B1
申请人: JCR PHARMACEUTICAL CO LTD
优先权: 2000
US
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