Biologics by McKesson Selected as Exclusive Pharmacy for Progeria Drug ZOKINVY
核心洞察
Biologics by McKesson (搜索) has been chosen by Sentynl Therapeutics (搜索) as the exclusive specialty pharmacy for ZOKINVY in the U.S.
ZOKINVY (lonafarnib) is the only FDA-approved treatment option for Hutchinson-Gilford Progeria Syndrome (搜索) and certain Progeroid Laminopathies (搜索).
This ultra-rare genetic disease affects approximately one in 18-20 million people in the United States, causing premature aging and mortality in children.
CARY, N.C. – Biologics by McKesson (搜索) has been selected by Sentynl Therapeutics (搜索) as the exclusive specialty pharmacy for ZOKINVY® (lonafarnib) in the United States. This appointment aims to streamline access and support for patients with Hutchinson-Gilford Progeria Syndrome (搜索) and processing-deficient Progeroid Laminopathies (搜索), who rely on this critical medication.
ZOKINVY, a farnesyltransferase inhibitor, is approved by the FDA for patients aged 12 months and older with a body surface area of 0.39 m2 and above. Its indications include reducing the risk of mortality in Hutchinson-Gilford Progeria Syndrome (搜索) and treating processing-deficient Progeroid Laminopathies (搜索) with specific genetic mutations. These mutations include Heterozygous LMNA (搜索) mutation with progerin-like protein accumulation, or homozygous or compound heterozygous ZMPSTE24 (搜索) mutations.
Hutchinson-Gilford Progeria Syndrome (搜索) is an ultra-rare genetic condition characterized by accelerated aging in children. The estimated prevalence in the United States is approximately one in 18 to 20 million people. The exclusive partnership between Sentynl and Biologics by McKesson (搜索) is designed to ensure that patients prescribed ZOKINVY receive prompt intervention and comprehensive management to optimize treatment outcomes.
"ZOKINVY is the first and only treatment option for Progeria," said Ela Lourido, vice president and general manager, Specialty Pharmacy Solutions, McKesson. "This is a groundbreaking milestone, and Biologics is honored to be chosen as the specialty pharmacy provider by Sentynl to offer this important medication to patients who need it."
Biologics by McKesson (搜索) emphasizes a patient-centric approach, providing specialized support through pharmacists with expertise in rare diseases, experienced nurses, and financial counselors. This multidisciplinary team assists patients in navigating financial assistance programs and accessing resources to support their treatment journey.