β-globin Restored Autologous HSC in β-thalassemia Major Patients

计划入组 2 人 · 首次发布于 2019 年 12 月 19 日

Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients

计划入组 10 人 · 首次发布于 2023 年 2 月 27 日

Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent Beta-thalassemia

计划入组 10 人 · 首次发布于 2023 年 3 月 17 日

β-globin restored autologous HSC(BRL Medicine Inc)

β-globin restored autologous HSC (Shenzhen Children'S Hospital)

β-globin restored autologous hematopoietic stem cells (Hemogen Gene)

RDC Global

Australia

Florin Iordache

Germany

Retina Global

United States

CRISPR-Based Casgevy Emerges as Preferred Gene Therapy for Beta-Thalassemia, Survey Shows

CorrectSequence Therapeutics Achieves First Successful Sickle Cell Disease Treatment in China Using Base Editing Technology CS-101

Transformer Base Editor Shows Promise in First Clinical Trial for β-Thalassaemia Treatment