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找到 3,531 条关于
“β-globin”
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3,531
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去年
CRISPR-Based Casgevy Emerges as Preferred Gene Therapy for Beta-Thalassemia, Survey Shows
去年
CorrectSequence Therapeutics Achieves First Successful Sickle Cell Disease Treatment in China Using Base Editing Technology CS-101
5个月前
Transformer Base Editor Shows Promise in First Clinical Trial for β-Thalassaemia Treatment
去年
Kanglin Biotechnology Secures $20 Million to Advance KL003 Gene Therapy for Beta Thalassemia and Sickle Cell Disease
3个月前
CorrectSequence's Base-Editing Therapy CS-206 Shows 15-Month VOC-Free Success in Sickle Cell Disease Patient
3年前
Mitapivat Shows Durable Improvements in Thalassemia Patients in Phase 2 Extension Study
去年
FDA Grants Orphan Drug Designation to Kind Pharmaceutical's AND017 for Sickle Cell Disease
去年
Oryzon Receives EMA Approval for First LSD1 Inhibitor Trial in Sickle Cell Disease
11天前
tBE Base Editing Therapy Achieves Durable Remission in Sickle Cell Disease and β-Thalassemia Across Diverse Genetic Backgrounds
5个月前
EpiFrontier Therapeutics Secures $32M AMED Grant to Advance First-in-Class G9a Inhibitor for Beta Globin Disorders
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