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找到 42,745 条关于
“ABCA-3 deficiency”
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42,745
临床试验
23,614
药物
4,857
机构
1,368
资讯
12,906
去年
FDA Grants Rare Pediatric Disease Designation to AlveoGene's AVG-002 for SP-B Deficiency
2年前
Grifols' Biotest Achieves Phase 3 Success for Fibrinogen Concentrate in Acquired Deficiency Treatment
去年
UCB's Fenfluramine Achieves Positive Phase 3 Results in Ultra-Rare CDKL5 Deficiency Disorder
去年
Agios' Mitapivat Achieves Primary Endpoint in Phase 3 Trial for Children with PK Deficiency
4个月前
BioMarin's BMN 401 Shows Mixed Results in Phase 3 Trial for Rare ENPP1 Deficiency
9个月前
UCB's Fenfluramine Shows Significant Seizure Reduction in Phase 3 Trial for CDKL5 Deficiency Disorder
6个月前
Ultragenyx Gene Therapy DTX301 Demonstrates Significant Ammonia Reduction in Phase 3 OTC Deficiency Trial
8个月前
FDA Expands Ferric Maltol Approval to Adolescents for Iron Deficiency Treatment
去年
FDA Approves Kebilidi, First Gene Therapy for AADC Deficiency
去年
FDA Approves Kebilidi, First Gene Therapy for AADC Deficiency
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