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找到 88 条关于
“Adrenoleukodystrophy”
全部
88
临床试验
56
药物
3
机构
0
资讯
29
去年
Adrenoleukodystrophy: Emerging Therapies Show Promise in Clinical Trials
上个月
CHMP Recommends Minoryx's NEZGLYAL as First Pharmacological Treatment for Pediatric Cerebral Adrenoleukodystrophy
去年
Minoryx and Neuraxpharm Submit New Marketing Authorization Application for Leriglitazone in Cerebral Adrenoleukodystrophy
去年
Viking Therapeutics' VK0214 Shows Promise in X-Linked Adrenoleukodystrophy Trial
去年
Bluebird Bio's Skysona Linked to Blood Cancers in Pediatric Patients
去年
EMA Initiates Accelerated Review for Bluebird's Gene Therapy Targeting Rare Disease CALD
去年
CHMP Rejects Neuraxpharm and Apellis Drugs, Companies to Appeal
去年
Minoryx Initiates Phase 2a Trial of Leriglitazone for Rett Syndrome
去年
Gene Therapy for CALD Shows Long-Term Efficacy but Carries Hematologic Cancer Risk
5年前
Bluebird Bio Announces Strategic Split into Separate Gene Therapy and Oncology Companies
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