Glycerol-Phenylbutyrate Treatment in Children With MCT Mutation (Allan-Herndon- Dudley Syndrome)

计划入组 6 人 · 首次发布于 2021 年 8 月 24 日

Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency

首次发布于 2023 年 6 月 22 日

Triac Trial II in MCT8 Deficiency Patients

计划入组 22 人 · 首次发布于 2015 年 3 月 24 日

Tiratricol(Emcitate)

C₁₄H₉I₃O₄

Leigh syndrome therapeutic(Leigh syndrome)

ORAI-XXXX

ALPORT SYNDROME FOUNDATION

United States

International Rett Syndrome Foundation

United States

RETT SYNDROME RESEARCH TRUST

United States

New International Guideline Published for Diagnosing and Treating Allan-Herndon-Dudley Syndrome

Egetis Therapeutics' Emcitate Poised for European Approval, Driving Optimistic Financial Outlook

FDA Leads Global Drug Approvals in 2024 with 50 Novel Medicines, Outpacing EMA's 46