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找到 64,755 条关于
“Arginase 1 Deficiency”
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64,755
临床试验
40,337
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7,403
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1,389
资讯
15,626
4年前
Aeglea BioTherapeutics Submits BLA for Pegzilarginase as First Potential Treatment for Arginase 1 Deficiency
去年
Intellia Therapeutics Initiates Phase 1/2 Trial of NTLA-3001 for AATD-Associated Lung Disease
去年
Beam Therapeutics Achieves Breakthrough in Base Editing for Alpha-1 Antitrypsin Deficiency
去年
FDA Approves Larger Vial Sizes of Takeda's GLASSIA for Alpha-1 Antitrypsin Deficiency
11个月前
Sanofi's Efdoralprin Alfa Achieves Primary Endpoints in Phase 2 Alpha-1 Antitrypsin Deficiency Study
9个月前
Regeneron Partners with Tessera in $275M Gene Editing Deal for Alpha-1 Antitrypsin Deficiency Treatment
去年
Prime Medicine Advances Gene Editing Program for Alpha-1 Antitrypsin Deficiency with 72% Correction Rate
7个月前
YolTech's YOLT-202 Gene Editing Therapy Shows Promising Results in Alpha-1 Antitrypsin Deficiency Trial
去年
Novel Therapies Poised to Revolutionize Alpha-1 Antitrypsin Deficiency Treatment
去年
UT Southwestern Scientists Develop Targeted Gene Therapy for Alpha-1 Antitrypsin Deficiency Using Designer Lipid Nanoparticles
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