Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Sickle Cell Disease

计划入组 5 人 · 首次发布于 2026 年 7 月 16 日

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

计划入组 10 人 · 首次发布于 2024 年 10 月 18 日

Putative Cognitive Enhancer VU319

计划入组 52 人 · 首次发布于 2017 年 7 月 18 日

BCL11A enhancer modified autologous hematopoietic stem cells (Edigene)

autophagy enhancer

utrophin expression enhancer

Intensity Therapeutics

United States

Ai-Media Technologies Ltd

United States

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