Charcot-Marie-Tooth Disease Type 1A(Metagenomi)

Charcot Marie Tooth -Type 2A (MitoRx Therapeutics)

Beclin activator peripheral (Charcot Marie Tooth disease type 1A)

mitofusin-2 agonists (oral, Charcot-Marie-Tooth type 2 disease)

SARM1 modulator (neurological disorders/Charcot Marie tooth disease type 1A)

PMP22 shRNA (non-viral vector/ARMM, Charcot-Marie Tooth 1A disease)

Recombinant Ebola Virus Disease Vaccine(Adenovirus Type 5 Vector)

Rx

MSDC-3G

Niemann-Pick Type C Disease(Alectos)

Niemann-Pick Type A disease therapeutics