Gene Therapy for Chronic Granulomatous Diseases - Long-term Follow-up

计划入组 14 人 · 首次发布于 1999 年 11 月 4 日

Lentiviral Gene Therapy for CGD

计划入组 10 人 · 首次发布于 2018 年 8 月 24 日

Whole Blood Biospecimen Collection for Subjects With Chronic Granulomatous Disease (CGD)

计划入组 6 人 · 首次发布于 2023 年 6 月 23 日

base-edited CD34+ HSPC (chronic granulomatous disease)

Chronic granulomatous disease therapy(Baxter International, Inc.)

NADPH oxidase stimulator(intravenous, chronic granulomatous disease)

Kineta Chronic Pain LLC

United States

Rare Disease Research, LLC

CASTLEMAN DISEASE COLLABORATIVE NETWORK

United States

World's First Gene Therapy for P47 Chronic Granulomatous Disease Shows Success in Teenage Patient

Prime Medicine's PM359 Gains FDA RMAT Designation for p47phox-Deficient Chronic Granulomatous Disease

Prime Medicine Reports Breakthrough Clinical Data for First Prime Editing Therapy in Chronic Granulomatous Disease