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找到 33,034 条关于
“Cincinnati Children’s Hospital”
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去年
Nancy Ratner Honored for Contributions to Neurofibromatosis Type 1 (NF1) Research
去年
Elixirgen Therapeutics Receives FDA Rare Pediatric Disease Designation for EXG-34217 in Dyskeratosis Congenita
去年
Infant Thriving After Gene Therapy for AADC Deficiency Following FDA Approval of KEBILIDI™
去年
KME-0584: Novel IRAK1/4 Inhibitor Shows Promise in AML and HR-MDS Treatment
2年前
Emapalumab Enhances Intervention-Free Survival in Pediatric HLH Patients Undergoing Stem Cell Transplant
去年
FDA Approves First Gene Therapy Directly Administered to the Brain for AADC Deficiency
2年前
Intrinsic Medicine Advances Human Milk Oligosaccharides (HMOs) for Chronic Disease Treatment
去年
Capricor Therapeutics Advances Deramiocel for Duchenne Muscular Dystrophy Cardiomyopathy
去年
Sangamo's Fabry Disease Gene Therapy ST-920 Receives Accelerated Approval Pathway from FDA
2年前
Capricor's CAP-1002 Shows Sustained Benefits in Duchenne Muscular Dystrophy After 3 Years
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