Hydrocortisone phosphate

C₂₁H₃₁O₈P

adrenal cortex extract

congenital hyperinsulinism therapeutic

hormone modulator (benign prostate hyperplasia)

congenital liver disease therapy

CRX gene therapy (Leber congenital amaurosis)

Congenital Dyserythropoietic Anemia(CDA)(CorrGene Biotechnology)

AAV8-AIPL1 gene therapy (Fondazione Telethon)

CEP-290

Congenital Isolated Hypoganglionosis cell therapy (Kidswell Bio)