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找到 25,274 条关于
“Cure Sanfilippo Foundation”
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25,274
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去年
Clemson Researchers Test Existing Drugs for Sanfilippo Syndrome Using Fruit Fly Models
去年
FDA Delays Gene Therapy Approval for Sanfilippo Syndrome Until 2026, Affecting Young Patients
去年
Spruce Biosciences Reports Breakthrough Long-Term Data for TA-ERT in Rare Sanfilippo Syndrome Type B
昨天
FDA Approves Fayuvi, First-Ever Gene Therapy for Sanfilippo Syndrome Type A
去年
Ultragenyx's UX111 Gene Therapy Shows Promise in Sanfilippo Syndrome Type A
去年
FDA Rejects Ultragenyx Gene Therapy for Sanfilippo Syndrome Over Manufacturing Concerns
11个月前
Spruce Biosciences' TA-ERT Receives FDA Breakthrough Therapy Designation for Ultra-Rare Sanfilippo Syndrome Type B
11个月前
Spruce Biosciences Secures $50M to Advance Sanfilippo Syndrome Type B Therapy Toward BLA Submission
去年
Ultragenyx's UX111 Gene Therapy for Sanfilippo Syndrome Type A Receives FDA Priority Review
9个月前
Spruce Biosciences Adds Commercial Veteran Keli Walbert to Board Ahead of Sanfilippo Syndrome Therapy BLA
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