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找到 32,811 条关于
“Cure Tay-Sachs Foundation”
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去年
UMass Chan Gene Therapy Shows Biochemical Correction in GM2 Gangliosidosis Phase I/II Trial
去年
MEDIPAL Holdings and JCR Pharmaceuticals Partner on Novel GM2 Gangliosidosis Therapy JR-479
8个月前
Azafaros to Present Phase 3 Nizubaglustat Data for Rare Lysosomal Storage Disorders at WORLDSymposium 2026
去年
Neurocrine Biosciences' Crenessity Receives FDA Approval for Congenital Adrenal Hyperplasia
3个月前
Royalty Pharma to Present at Goldman Sachs 47th Annual Global Healthcare Conference
3个月前
Azafaros Publishes Phase 2 RAINBOW Study Data for Nizubaglustat in GM2 Gangliosidosis and Niemann-Pick Type C Disease
3个月前
Upstream Bio to Present Novel TSLP Antagonist Verekitug at Goldman Sachs Healthcare Conference
去年
Goldman Sachs Downgrades Dynavax on Competitive Pressures in Shingles and Hepatitis B Markets
去年
Azafaros to Present at J.P. Morgan's 43rd Annual Healthcare Conference
上个月
Andelyn Biosciences Partners with Queen's University to Manufacture AAV9-GM2 Gene Therapy for GM2 Gangliosidoses
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