Natural History Study Protocol in PMM2-CDG (CDG-Ia)

计划入组 139 人 · 首次发布于 2017 年 6 月 1 日

Acetazolamide Efficacy in Ataxia in PMM2-CDG

计划入组 25 人 · 首次发布于 2020 年 12 月 22 日

Study of ORL-1M (D-mannose) in Patients With CDG-Ib

计划入组 5 人 · 首次发布于 2018 年 1 月 19 日

CGS-27023A

AVTX-802

Fucose

C₆H₁₂O₅

CDC ENTEBBE

Uganda

CDR-Life AG

Switzerland

COG Financial Services Ltd

Drug repurposing screen identifies dopamine signaling and COX inhibition as candidate therapeutic pathways for PIGA-CDG

FDA Grants Fast Track Designation to Glycomine's GLM101 for PMM2-CDG Treatment

Glycomine Secures $115M Series C Funding to Advance Novel Treatment for PMM2-CDG Rare Disease