European Registry on Rare Neurological Diseases

计划入组 5,000 人 · 首次发布于 2020 年 3 月 24 日

COVID-19 and Rare Skin Diseases European Observational Study During an Epidemic

计划入组 80 人 · 首次发布于 2020 年 6 月 30 日

Clinical and Genetic Examination of Usher Syndrome Patients' Cohort in Europe

计划入组 100 人 · 首次发布于 2013 年 10 月 7 日

RARE DISEASES(Gero)

European pilchard

rare phytocannabinoids (skin diseases)

RECORDATI RARE DISEASES

France

Recordati Rare Diseases, Inc.

United States

HRA Pharma Rare Diseases SAS

France

Thryv Therapeutics Unveils Breakthrough SGK1 Inhibitor Data for Heart Failure and Long QT Syndrome at ESC Congress 2025

OXB Selected as GMP Manufacturing Partner for Plowshare Therapies' AAV Gene Therapy Programme Targeting Rare Genetic Diseases

Recordati Rare Diseases Presents Nine Research Studies on Rare Hematologic Disorders at ASH 2025