Finding Genes for Rare Diseases

首次发布于 2016 年 3 月 31 日

RAHM Foundation Retrospective Study of Various Diseases

计划入组 10,000 人 · 首次发布于 2015 年 2 月 10 日

FACE for Children With Rare Diseases

计划入组 42 人 · 首次发布于 2021 年 4 月 22 日

RARE DISEASES(Gero)

rare phytocannabinoids (skin diseases)

Rare mitochondrial diseases(MitoCareX)

RECORDATI RARE DISEASES

France

Recordati Rare Diseases, Inc.

United States

HRA Pharma Rare Diseases SAS

France

US House Passes Bipartisan Bill to Reauthorize FDA's Rare Pediatric Disease Priority Review Voucher Program

PacBio Partners with n-Lorem Foundation and EspeRare to Advance Personalized ASO Therapies for Ultra-Rare Genetic Diseases

Gates Foundation Funds Likarda's Novel Antibody-Secreting Cell Therapy for Infectious Diseases