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找到 8,299 条关于
“FSHD Canada Foundation”
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3天前
FDA Clears Satellos IND for Forazapadin in FSHD, Phase 2 Trial Set for Q4 2026
去年
Avidity Biosciences Initiates Biomarker Cohort in Phase 1/2 FORTITUDE Trial for FSHD Therapy
去年
First-in-Human Gene Therapy Trial Launches for Rare Muscle Disorder FSHD
去年
Springbok Analytics Pioneers AI-Driven MRI Analysis in Landmark Pediatric FSHD Study
去年
Avidity Biosciences' Del-brax Trial Enrolls New Cohort for Accelerated FSHD Approval
去年
Dyne Therapeutics Reports Breakthrough Preclinical Results for FSHD Gene Therapy DYNE-302
去年
Epicrispr Biotechnologies Secures $68 Million to Advance First Epigenetic Therapy for FSHD
5个月前
FSHD Society Launches Industry Collaborative to Accelerate Clinical Trial Development for Rare Muscular Dystrophy
去年
SOLVE FSHD Partners with Modalis to Develop CRISPR-Based Epigenome Editing Therapy for Muscular Dystrophy
3个月前
From Patient to Pioneer: How FSHD Researchers Are Redefining a Rare Disease Through Epigenetics and CRISPR
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