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找到 552 条关于
“Fmr1”
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552
临床试验
526
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13
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13
去年
QurAlis Secures Exclusive License for Novel RNA-Targeted Therapy in Fragile X Syndrome
12个月前
Harmony Biosciences' ZYN002 Phase 3 Trial Fails to Meet Primary Endpoint in Fragile X Syndrome
上个月
Marvel Biosciences' MB-204 Reverses Behavioural and Cognitive Deficits in Fragile X Mouse Model, Marking Third Preclinical ASD Success
9个月前
Mirum Pharmaceuticals Initiates Phase II Trial of MRM-3379 for Fragile X Syndrome
2年前
Two Major Breakthroughs in Fragile X Syndrome Treatments
2年前
Spinogenix Receives FDA Orphan Drug Designation for SPG601 to Treat Fragile X Syndrome
去年
Fragile X Syndrome Market Set for $83.2M Growth with Novel Therapeutic Approaches
去年
Spinogenix's SPG601 Shows Promise in Phase 2 Trial for Fragile X Syndrome
2年前
FDA Grants Orphan Drug Status to Spinogenix's SPG601 for Fragile X Syndrome
3个月前
JW Pharmaceutical's DDC-02 Restores Cognitive Function Across Multiple Rare Neurodevelopmental Disorder Models, Targets 2028 Clinical Trials
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