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找到 90,388 条关于
“Gaucher's disease”
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90,388
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67,755
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Gaucher's disease therapy (Immusoft)
Exosome-based Gaucher's disease Type-II enzyme therapeutic (ILIAS Biologics)
liver disease program
siRNA therapeutics for ocular disease/dermatological disease (Phio Pharmaceuticals)
undisclosed drug (fibrotic liver disease/NASH), Engitix/Takeda
chronic kidney disease therapy
undisclosed rare disease therapeutic (rare disease/eye disease/skin disease)
gene therapy (Gaucher’s disease)
Monocyte Locomotion Inhibitory Factor (Immune Disease Institute)
Huntington's disease program (Huntington's disease)
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