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找到 102,381 条关于
“Kleefstra syndrome type 1”
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102,381
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2个月前
Biallelic EHMT2 Variants Identified in Second-Ever Case of Autosomal Recessive Kleefstra-Like Neurodevelopmental Syndrome
3个月前
IDefine Partners with UT Southwestern to Develop First Gene Therapy for Kleefstra Syndrome
去年
AAVantgarde Reports Positive Phase 1/2 Data for Gene Therapy AAVB-081 in Usher Syndrome Type 1B
去年
Ultragenyx's UX111 Gene Therapy Shows Promise in Sanfilippo Syndrome Type A
2年前
Gilead's Lenacapavir Shows Promise in HIV Prevention, While GLP-1s Studied for Type 1 Diabetes
昨天
FDA Approves Fayuvi, First-Ever Gene Therapy for Sanfilippo Syndrome Type A
去年
AAVantgarde Bio Doses First Patient in Phase 1/2 Trial of AAVB-081 for Usher Syndrome Type 1B
去年
World-First Gene Therapy Restores Vision in Patient with Usher Syndrome Type 1B
11个月前
JR-446 Receives Japanese Orphan Drug Designation for Rare Sanfilippo Syndrome Type B
去年
Sana Biotechnology's Breakthrough in Type 1 Diabetes Treatment
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