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找到 80 条关于
“LCA4”
全部
80
临床试验
46
药物
25
机构
0
资讯
9
去年
MeiraGTX's Gene Therapy Shows Promising Visual Benefits in Children with Rare Genetic Blindness
去年
MeiraGTx Advances Gene Therapy Pipeline with FDA RMAT Designation and Pivotal Trial Progress
去年
MeiraGTx and Hologen AI Form $430 Million Strategic Collaboration to Advance Parkinson's Disease Gene Therapy
5个月前
MeiraGTx Receives FDA Breakthrough Therapy Designation for Gene Therapy Treating Radiation-Induced Dry Mouth
去年
Opus Genetics to Present 6-Month Data on OPGx-LCA5 Gene Therapy for LCA5-Associated Inherited Retinal Disease
2年前
Gene Therapy Shows Promise in Restoring Vision for LCA1 Patients
去年
EMA Provides Positive Feedback on ABIONYX Pharma's CER-001 for LCAT Deficiency
去年
Atsena Therapeutics and Nippon Shinyaku Partner to Advance Gene Therapy for LCA1
去年
Opus Genetics Advances LCA5 Gene Therapy Program with First Pediatric Patient Dosing and Promising Adult Data