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找到 80,245 条关于
“Leber congenital amaurosis type 1”
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2年前
Gene Therapy Shows Promise in Restoring Vision for LCA1 Patients
6年前
First In Vivo CRISPR Therapy Dosed in Clinical Trial for Congenital Blindness
去年
Atsena Therapeutics Secures $150M Series C Funding to Advance Ocular Gene Therapies for Inherited Blindness
2年前
Atsena Therapeutics Reports Promising Results for XLRS Gene Therapy Using Novel Spreading Capsid
2年前
CRISPR Gene Editing Shows Promise in Treating Rare Form of Blindness
6天前
Editas Medicine Targets 2026 Patient Dosing for In Vivo CRISPR LDL Therapy EDIT-401
4个月前
Six-Year-Old Girl Regains Vision Through Groundbreaking NHS Gene Therapy for Leber's Congenital Amaurosis
去年
HuidaGene's CRISPR/Cas13 RNA-Editing Therapy HG202 Cleared for US Trial in Macular Degeneration
去年
Ocugen to Highlight Retinal Gene Therapy Progress at Clinical Showcase
去年
Ocugen's OCU400 Gene Therapy Shows Promise in Retinitis Pigmentosa Phase 1/2 Trial
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