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找到 50 条关于
“MBNL”
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50
临床试验
32
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资讯
6
6个月前
ARTHEx Biotech Receives FDA Fast Track Designation for ATX-01 in Myotonic Dystrophy Type 1
去年
ARTHEx Biotech Secures $87M Series B to Advance Novel RNA Therapy for Myotonic Dystrophy Type 1
去年
Vidofludimus Calcium Phase 3 Trials Continue, Eplontersen Recommended for Approval, and ATX-01 Phase 1/2 Trial Begins
10个月前
PepGen Secures U.S. Patent for PGN-EDODM1, Advancing Myotonic Dystrophy Type 1 Treatment
11个月前
PepGen's DM1 Therapy Achieves Record 53.7% Splicing Correction in Phase 1 Trial
5个月前
Shionogi's Cefiderocol Shows 68% Clinical Cure Rate Against Highly Resistant MBL-Producing Enterobacterales in Real-World Study