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找到 74,740 条关于
“MPS II (Hunter syndrome)”
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74,740
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去年
JCR Pharmaceuticals Launches Phase III Trial of Long-Acting Growth Hormone JR-142 in Japan
2年前
Denali Therapeutics Announces Positive Clinical Updates and Financial Results for Q1 2024
去年
REGENXBIO and Nippon Shinyaku Partner to Advance Gene Therapies for MPS I and MPS II
去年
JCR Pharmaceuticals Licenses JUST-AAV Gene Therapy Platform to Alexion in $825 Million Deal
11个月前
JCR Pharmaceuticals' JUST-AAV Platform Achieves 52-Fold Improvement in Muscle Gene Delivery While Reducing Liver Exposure
7年前
Denali's Hunter Syndrome Candidate Receives FDA Orphan Drug and Rare Pediatric Disease Designations
去年
JCR Pharmaceuticals Completes Enrollment in Global Phase III Trial for Blood-Brain Barrier-Penetrating Hunter Syndrome Therapy
8个月前
Italfarmaco and JCR Pharmaceuticals Form Strategic Partnership to Commercialize Givinostat for Duchenne Muscular Dystrophy in Japan
9个月前
Immusoft Receives FDA Orphan Drug Designation for Engineered B Cell Therapy ISP-002 in Hunter Syndrome
2年前
Denali Therapeutics Plans Accelerated Approval Filing for Tividenofusp Alfa in MPS II
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